PhD in Biomedical Sciences and Biotechnology

Home –  PhD students –  Faculty –  Seminars

1. A. Branchini, M. Baroni, F. Burini, F. Puzzo, F. Nicolosi, R. Mari, R. Gemmati, F. Bernardi, M. Pinotti (2015) The carboxyl-terminal region is NOT essential for secreted and functional levels of coagulation factor X. Journal of Thrombosis and Haemostasis
2. E. Masat, P. Laforêt, M. De Antonio, G. Corre, B. Perniconi, N. Taouagh, K. Mariampillai, D. Amelin, W. Mauhin, J.Y. Hogrel, C. Caillaud, G. Ronzitti, F. Puzzo, K. Kuranda, P. Colella, R. Mallone, O. Benveniste, F. Mingozzi (2016) Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients. Scientific reports
3. M. Hösel, A. Huber, S. Bohlen, J. Lucifora, G. Ronzitti, F. Puzzo, F. Boisgerault, U.T. Hacker, W.J. Kwanten, N. Klöting, M. Blüher, A. Gluschko, M. Schramm, O. Utermöhlen, W. Bloch, F. Mingozzi, O. Krut, H. Büning (2017) Autophagy Determines Efficiency of Liver-directed Gene Therapy with Adeno-associated Viral Vectors. Hepatology
4. F. Puzzo, P. Colella, M. G. Biferi, D. Bali, N. K. Paulk, P. Vidal, F. Collaud, M. Simon-Sola, S. Charles, R. Hardet, C. Leborgne, A. Meliani,, M. Cohen-Tannoudji, S. Astord, B. Gjata, P. Sellier, L. van Wittenberghe, A. Vignaud, F. Boisgerault, M. Barkats, P. Laforet, M. A. Kay, D. D. Koeberl, G. Ronzitti, F. Mingozzi (2017) Whole-body rescue of Pompe disease with AAV liver delivery of engineered secretable GAA transgenes. Science translational medicine In press